Many gene therapies for hemophilia are being studied in people to determine if they are safe and effective. This educational website will not focus on any commercially available products or specific gene therapies being researched for hemophilia A or B.
This site is an educational service brought to you by BioMarin and is intended for healthcare professionals in the US. Many gene therapies for hemophilia A and B are being studied in people to determine if they are safe and effective. No gene therapies for hemophilia have been approved for use or determined to be safe or effective.