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What causes genetic conditions?

How are investigational gene transfer therapies designed to work inside the body?

What is gene transfer therapy research designed to do?

Spot and Pop the Mutations

Mutations can come in multiple forms and are responsible for most genetic conditions, including hemophilia A or B and cystic fibrosis. Play our simple game, Mutation Pop, to identify four of the most common forms of genetic mutations that can lead to genetic conditions:

  • Errors in a single strand of DNA
  • A repeated DNA sequence
  • Added DNA where it doesn’t belong
  • Missing pieces of DNA

In this game you will have to quickly spot the mutated genes and pop as many as possible while allowing the functional genes to pass through. Find out if you have what it takes to earn the highest score!

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Get to know the gene therapy research terms

See Glossary

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