Turning
complexity
into clarity

An understandable resource on gene therapy research

Gene Therapy Research

What are you curious about?

What Is gene therapy?

What are the steps involved with gene transfer therapy?

What causes genetic conditions?

What are the goals of gene transfer therapy research?

What are the possible risks of gene therapy research?

Upcoming Virtual Event

Florida Hemophilia Association Program on Gene Therapy Research

Presented by:

Joanna Davis, MD

Medical Director of Pediatric Comprehensive Hemophilia Treatment

University of Miami Leonard Miller School of Medicine

09/26/20

See Event Details

View all upcoming events

SO…WHO IS HEMDIFFERENTLY?

Our goal is to make the conversation around gene therapy research honest, accurate, and fun.

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Turning complexity into clarity