Turning
complexity
into clarity

An understandable resource on gene therapy research

Gene Therapy Research

What are you curious about?

What Is gene therapy?

What are the steps involved with gene transfer therapy?

What causes genetic conditions?

What are the goals of gene transfer therapy research?

What are the possible risks of gene therapy research?

Upcoming Virtual Event

Gene Therapy Jeopardy with Midwest Hemophilia Association

Presented by:

Michael F. Guerrera, MD
Director, Comprehensive Hemostasis and Thrombosis Program
Children’s National Hospital

05/20/21

See Event Details

View all upcoming events

SO…WHAT IS HEMDIFFERENTLY ALL ABOUT?

Gene therapy research is a topic on many minds. Our goal is to make the conversation around gene therapy research honest, accurate, and fun.

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