Skip to main content
HemDifferently
HemDifferently
  • Gene Therapy Research
    • What is gene therapy?
    • What are the steps involved with gene transfer therapy?
    • What Causes Genetic Conditions?
    • What are the Goals of Gene Transfer Therapy Research?
    • What are the Possible Risks of Gene Therapy Research?
  • Resources
    • Resources
    • Glossary
  • Events
  • About
  • Sign Up
  • For Healthcare Providers
  • English/Spanish
  • Gene Therapy Research
    • What is gene therapy?
    • What are the steps involved with gene transfer therapy?
    • What Causes Genetic Conditions?
    • What are the Goals of Gene Transfer Therapy Research?
    • What are the Possible Risks of Gene Therapy Research?
  • Resources
    • Resources
    • Glossary
  • Events
  • About
  • Sign Up
  • For Healthcare Providers
  • English/Spanish

Site Map

  • Home
  • What Is Gene Therapy?
  • What Are the Steps Involved with Gene Transfer Therapy?
  • What Causes Genetic Conditions?
  • What Are the Goals of Gene Transfer Therapy?
  • What are the Possible Risks of Gene Therapy?
  • Resources
  • Events
  • Glossary
  • About
  • Sign Up
  • Practical Considerations: for Healthcare Professionals
  • Resources: for Healthcare Professionals
  • Sign Up: for Healthcare Professionals
  • Site Map
  • Privacy Policy
  • Terms of Use
  • Sign Up
  • Site Map
  • Contact Us
  • Terms of Use
  • Glossary
  • Privacy Policy
  • HCP
  • Cookie Preferences
Many gene therapies for hemophilia are being studied in people to determine if they are safe and effective. This educational website will not focus on any commercially available products or specific gene therapies being researched for hemophilia A or B. This site and the contents within were created for educational purposes only. The content is not prescriptive and should not replace consultation with a trained healthcare provider. Information regarding gene therapy is provided as a general overview and is not comprehensive.
© 2023 BioMarin Pharmaceutical Inc. All rights reserved. US-HEM-00230 04/23

Many gene therapies for hemophilia are being studied in people to determine if they are safe and effective. This educational website will not focus on any commercially available products or specific gene therapies being researched for hemophilia A or B.

×

This site is an educational service brought to you by BioMarin and is intended for healthcare professionals in the US. Many gene therapies for hemophilia A and B are being studied in people to determine if they are safe and effective. No gene therapies for hemophilia have been approved for use or determined to be safe or effective.

This website uses cookies to improve website functionality. By using this website, you consent to our use of cookies. For more information, please see our Privacy Policy and Terms and Conditions.

I am a US healthcare professional
×

You’ve opted in to receive information by phone, please provide your phone number.

×

Please opt-in to receiving phone communication.

×

Please enter the 10-digit phone number.

×