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HemDifferently
HemDifferently
  • Gene Therapy Research
    • What is gene therapy?
    • What are the steps involved with gene transfer therapy?
    • What Causes Genetic Conditions?
    • What are the Goals of Gene Transfer Therapy Research?
    • What are the Possible Risks of Gene Therapy Research?
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  • Gene Therapy Research
    • What is gene therapy?
    • What are the steps involved with gene transfer therapy?
    • What Causes Genetic Conditions?
    • What are the Goals of Gene Transfer Therapy Research?
    • What are the Possible Risks of Gene Therapy Research?
  • Resources
    • Resources
    • Glossary
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  • About
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Many gene therapies for hemophilia are being studied in people to determine if they are safe and effective. No gene therapies for hemophilia have been approved for use. This site and the contents within were created for educational purposes only. The content is not prescriptive and should not replace consultation with a trained healthcare provider. Information regarding gene therapy is provided as a general overview and is not comprehensive.
© 2021 BioMarin Pharmaceutical Inc. All rights reserved. MMRC-GTH-0302 04/20

This site is an educational service brought to you by BioMarin and is intended for US residents only. Many gene therapies for hemophilia A and B are being studied in people to determine if they are safe and effective. No gene therapies for hemophilia have been approved for use or determined to be safe or effective.

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This site is an educational service brought to you by BioMarin and is intended for healthcare professionals in the US. Many gene therapies for hemophilia A and B are being studied in people to determine if they are safe and effective. No gene therapies for hemophilia have been approved for use or determined to be safe or effective.

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