Turning
complexity
into clarity

An understandable resource on gene therapy research

Gene Therapy Research

What are you curious about?

What Is gene therapy?

What are the steps involved with gene transfer therapy?

What causes genetic conditions?

What are the goals of gene transfer therapy research?

What are the possible risks of gene therapy research?

Upcoming Virtual Event

Bleeding Disorders Foundation of Washington Program on Gene Therapy Research

Presented by:

Doris Quon, MD, PhD

Medical Director, Orthopaedic Hemophilia Treatment Center

Orthopaedic Institute for Children

01/21/21

See Event Details

View all upcoming events

SO…WHO IS HEMDIFFERENTLY?

Our goal is to make the conversation around gene therapy research honest, accurate, and fun.

Let’s Dive In!

Get information and updates delivered right to your inbox

Email Address

Are you a U.S. resident?

This website is intended for US participants only.

Yes

First Name

Last Name

Email Address

Phone Number

Zip Code

By checking this box and clicking SUBMIT below, I confirm I am at least 18 years old; confirm I agree to BioMarin’s Privacy Policy and CCPA Notice and Terms of Use; consent to BioMarin, its successors, agents, and/or assigns using the email address I have provided to keep me informed about news and developments, market research or surveys, or other opportunities that may be of interest to me; and confirm I understand these communications/materials may contain information that markets or advertises BioMarin products, goods, or services.

By checking this box and clicking SUBMIT below, I consent to BioMarin, its successors, agents, and/or assigns using the phone number I have provided to phone and/or text me with communications/messages that contain information marketing BioMarin’s products, goods, or services, including via use of an automatic telephone dialing system; and confirm I understand I am not required to provide my consent as a condition of purchasing or renting any products, goods, or services.

Please Verify Captcha!

Turning complexity into clarity