BioMarin offers educational gene therapy research programs for all audiences
One-hour, educational programs led by trained healthcare professionals for those seeking to better understand gene therapy research.
It’s important for all members of the community to understand what makes gene therapy research different from other types of research, from the research process and technology, to the technical and practical requirements. We created HemDifferently as an educational platform to help guide understanding of what makes gene therapy unique.
Today, many gene therapies are being studied in people to determine if they are safe and effective. The ongoing research may present different requirements for healthcare providers and patients. Below are some potential practical considerations for addressing as your institution considers gene therapy.
Each gene therapy will be evaluated by the FDA upon submission. No gene therapy for hemophilia A or B has been determined to be safe or effective or approved for use.
Site readiness
Infrastructure, training, business, and administrative considerations
Patient conversations
Setting appropriate patient expectations
Patient identification
Determining a patient's candidacy for different gene therapies
Insurance process
Understanding access considerations
Dosage and administration
Protocols to administer gene therapies
Patient monitoring
Short- and long-term follow-up
One-hour, educational programs led by trained healthcare professionals for those seeking to better understand gene therapy research.
1. Learn with your Colleagues + Peers
BioMarin’s gene therapy learning academy offers in-person or virtual interactive programs led by trained healthcare professionals.
2. Educate your Patients
One-hour, educational programs led by trained healthcare professionals for those seeking to better understand gene therapy research.
Want to learn more about educational programming?